Intracellular biologics pipeline

Using our proprietary EEV™ technology, we are creating a pipeline of oligonucleotide therapies to treat neuromuscular diseases including Duchenne muscular dystrophy (DMD). Our other intracellular programs span multiple therapeutic areas and focus on biologics including antibodies, peptides, enzymes and proteins.

Oligonucleotides
Neuromuscular
Duchenne Muscular Dystrophy
Preclinical
Duchenne Muscular Dystrophy
Discovery
Other Neuromuscular Diseases
Discovery
Beyond Neuromuscular
Additional Diseases
Discovery
Antibodies and Peptides
Multiple Therapeutic Areas
Oncology
Discovery
Additional Diseases
Discovery
Enzymes and Proteins
Inborn Errors of Metabolism
MNGIE
Preclinical